
- A UPMC doctor waited years for a needed drug to get approval. The FDA finally gave it Pittsburgh Post-Gazette
 - FDA greenlights Stealth Bio’s injection as 1st treatment for Barth syndrome Fierce Pharma
 - FDA gives approval for treatment of rare disease affecting Hall Co. family AccessWdun
 - US FDA approves first treatment for rare, life-threatening disease in males Reuters
 - Stealth Wins Expedited FDA Nod for First-Ever Barth Syndrome Treatment BioSpace
 
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